![“The SINE compound KPT-350 blocks dystrophic pathologies in DMD zebrafish and mice”]()
“The SINE compound KPT-350 blocks dystrophic pathologies in DMD zebrafish and mice”Hightower, Rylie M.; Reid, Andrea L.; Gibbs, Devin E.; Wang, Yimin; Widrick, Jeffrey J.; Kunkel, Louis M.; Kastenschmidt, Jenna M.; Villalta, S. Armando; van Groen, Thomas; Chang, Hua; Gornisiewicz, Savanna; Landesman, Yosef; Tamir, Sharon; Alexander, Matthew S. · Molecular Therapy · 2019