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NEW THERAPEUTIC APPROACHES AND THEIR READOUTNagaraju, K.; Vila, M.; Novak, J.; Boehler, J.; Hogarth, M.; Zhang, A.; Kinder, T.; Mazala, D.; Benny Klimek, M.; Fiorillo, A.; van den Anker, J.; Hathout, Y.; Hoffman, E.; Partridge, T. · Neuromuscular Disorders · 2018