563. Correction of Glycogen Storage Disease Type II by Systemic Delivery of an AAV2/8 Vector Containing a Muscle-Specific Promoter
Sun, Baodong; Li, Ping; Talmage, Brown; Andrew, Bird; Yan, Zhen; Koeberl, Dwight D.
- 期刊名称Molecular Therapy
- 作者Sun, Baodong; Li, Ping; Talmage, Brown; Andrew, Bird; Yan, Zhen; Koeberl, Dwight D.
- 卷第13卷
- 印刷ISSN1525-0016
- 文件大小89.26KB
- 发表时间2006-5
- DOI10.1016/j.ymthe.2006.08.636