410. Physiological Correction of Glycogen Storage Disease Type II Using Adeno-Associated Virus Serotype 1 Vectors
Mah, Cathryn; Pacak, Christina A.; Cresawn, Kerry O.; DeRuisseau, Lara R.; Germain, Sean; Lewis, Melissa A.; Fuller, David D.; Byrne, Barry J.
- 期刊名称Molecular Therapy
- 作者Mah, Cathryn; Pacak, Christina A.; Cresawn, Kerry O.; DeRuisseau, Lara R.; Germain, Sean; Lewis, Melissa A.; Fuller, David D.; Byrne, Barry J.
- 卷第13卷
- 印刷ISSN1525-0016
- 文件大小82.49KB
- 发表时间2006-5
- DOI10.1016/j.ymthe.2006.08.473