The risks of therapeutic misconception and individual patient (n = 1) “trials” in rare diseases such as Duchenne dystrophy
Annemieke Aartsma-Rus; Pat Furlong; Elizabeth Vroom; Gert-Jan van Ommen; Erik Niks; Chiara Straathof; Jan Verschuuren; Annemieke Aartsma-Rus; Alessandra Ferlini; Lynn Hagger; Emma Heslop; Veronika Karcagi; Jan Kirschner; Pauline McCormack; Pat Moeschen; Francesco Muntoni; Marie-Christine Ouillade; Jes Rahbeck; Christoph Rehmann-Sutter; Francoise Rouault; Tomas Sejersen; Elizabeth Vroom; Simon Woods
- 作者Annemieke Aartsma-Rus; Pat Furlong; Elizabeth Vroom; Gert-Jan van Ommen; Erik Niks; Chiara Straathof; Jan Verschuuren; Annemieke Aartsma-Rus; Alessandra Ferlini; Lynn Hagger; Emma Heslop; Veronika Karcagi; Jan Kirschner; Pauline McCormack; Pat Moeschen; Francesco Muntoni; Marie-Christine Ouillade; Jes Rahbeck; Christoph Rehmann-Sutter; Francoise Rouault; Tomas Sejersen; Elizabeth Vroom; Simon Woods
- 卷第21卷
- 期第1期
- 印刷ISSN0960-8966
- 文件大小91.10KB
- 发表时间2011
- DOI10.1016/j.nmd.2010.09.012