Lentiviral mediated stem cell gene therapy corrects a mouse model of mucopolysaccharidosis type IIIA
Brian Bigger; Alex Langford-Smith; Fiona Wilkinson; Kia Langford-Smith; Ana Sergijenko; Ed Wraith; Rob Wynn
- 作者Brian Bigger; Alex Langford-Smith; Fiona Wilkinson; Kia Langford-Smith; Ana Sergijenko; Ed Wraith; Rob Wynn
- 卷第102卷
- 期第2期
- 印刷ISSN1096-7192
- 电子ISSN1096-7206
- 文件大小58.11KB
- 发表时间2011
- DOI10.1016/j.ymgme.2010.11.026