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Application of Mutated miR-206 Target Sites Enables Skeletal Muscle-specific Silencing of Transgene Expression of Cardiotropic AAV9 Vectors

Application of Mutated miR-206 Target Sites Enables Skeletal Muscle-specific Silencing of Transgene Expression of Cardiotropic AAV9 Vectors

Geisler, Anja; Schön, Christian; Größl, Tobias; Pinkert, Sandra; Stein, Elisabeth A; Kurreck, Jens; Vetter, Roland; Fechner, Henry
  • 期刊名称Molecular Therapy
  • 作者Geisler, Anja; Schön, Christian; Größl, Tobias; Pinkert, Sandra; Stein, Elisabeth A; Kurreck, Jens; Vetter, Roland; Fechner, Henry
  • 卷第21卷
  • 期第5期
  • 印刷ISSN1525-0016
  • 电子ISSN1525-0024
  • 文件大小752.24KB
  • 发表时间2013-5
  • DOI10.1038/mt.2012.276
  • 页码924-933
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