Application of Mutated miR-206 Target Sites Enables Skeletal Muscle-specific Silencing of Transgene Expression of Cardiotropic AAV9 Vectors
Geisler, Anja; Schön, Christian; Größl, Tobias; Pinkert, Sandra; Stein, Elisabeth A; Kurreck, Jens; Vetter, Roland; Fechner, Henry
- 期刊名称Molecular Therapy
- 作者Geisler, Anja; Schön, Christian; Größl, Tobias; Pinkert, Sandra; Stein, Elisabeth A; Kurreck, Jens; Vetter, Roland; Fechner, Henry
- 卷第21卷
- 期第5期
- 印刷ISSN1525-0016
- 电子ISSN1525-0024
- 文件大小752.24KB
- 发表时间2013-5
- DOI10.1038/mt.2012.276
- 页码924-933