Eteplirsen for the treatment of Duchenne muscular dystrophy
Mendell, Jerry R.; Rodino-Klapac, Louise R.; Sahenk, Zarife; Roush, Kandice; Bird, Loren; Lowes, Linda P.; Alfano, Lindsay; Gomez, Ann Maria; Lewis, Sarah; Kota, Janaiah; Malik, Vinod; Shontz, Kim; Walker, Christopher M.; Flanigan, Kevin M.; Corridore, Marco; Kean, John R.; Allen, Hugh D.; Shilling, Chris; Melia, Kathleen R.; Sazani, Peter; Saoud, Jay B.; Kaye, Edward M.
- 期刊名称Annals of Neurology
- 作者Mendell, Jerry R.; Rodino-Klapac, Louise R.; Sahenk, Zarife; Roush, Kandice; Bird, Loren; Lowes, Linda P.; Alfano, Lindsay; Gomez, Ann Maria; Lewis, Sarah; Kota, Janaiah; Malik, Vinod; Shontz, Kim; Walker, Christopher M.; Flanigan, Kevin M.; Corridore, Marco; Kean, John R.; Allen, Hugh D.; Shilling, Chris; Melia, Kathleen R.; Sazani, Peter; Saoud, Jay B.; Kaye, Edward M.
- 卷第74卷
- 期第5期
- 印刷ISSN0364-5134
- 文件大小623.53KB
- 发表时间2013-11
- DOI10.1002/ana.23982
- 页码637-647