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Eteplirsen for the treatment of Duchenne muscular dystrophy

Eteplirsen for the treatment of Duchenne muscular dystrophy

Mendell, Jerry R.; Rodino-Klapac, Louise R.; Sahenk, Zarife; Roush, Kandice; Bird, Loren; Lowes, Linda P.; Alfano, Lindsay; Gomez, Ann Maria; Lewis, Sarah; Kota, Janaiah; Malik, Vinod; Shontz, Kim; Walker, Christopher M.; Flanigan, Kevin M.; Corridore, Marco; Kean, John R.; Allen, Hugh D.; Shilling, Chris; Melia, Kathleen R.; Sazani, Peter; Saoud, Jay B.; Kaye, Edward M.
  • 期刊名称Annals of Neurology
  • 作者Mendell, Jerry R.; Rodino-Klapac, Louise R.; Sahenk, Zarife; Roush, Kandice; Bird, Loren; Lowes, Linda P.; Alfano, Lindsay; Gomez, Ann Maria; Lewis, Sarah; Kota, Janaiah; Malik, Vinod; Shontz, Kim; Walker, Christopher M.; Flanigan, Kevin M.; Corridore, Marco; Kean, John R.; Allen, Hugh D.; Shilling, Chris; Melia, Kathleen R.; Sazani, Peter; Saoud, Jay B.; Kaye, Edward M.
  • 卷第74卷
  • 期第5期
  • 印刷ISSN0364-5134
  • 文件大小623.53KB
  • 发表时间2013-11
  • DOI10.1002/ana.23982
  • 页码637-647
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