Recombination-activating gene 1 (Rag1)–deficient mice with severe combined immunodeficiency treated with lentiviral gene therapy demonstrate autoimmune Omenn-like syndrome
van Til, Niek P.; Sarwari, Roya; Visser, Trudi P.; Hauer, Julia; Lagresle-Peyrou, Chantal; van der Velden, Guus; Malshetty, Vidyasagar; Cortes, Patricia; Jollet, Arnaud; Danos, Olivier; Cassani, Barbara; Zhang, Fang; Thrasher, Adrian J.; Fontana, Elena; Poliani, Pietro L.; Cavazzana, Marina; Verstegen, Monique M.A.; Villa, Anna; Wagemaker, Gerard
- 期刊名称Journal of Allergy and Clinical Immunology
- 作者van Til, Niek P.; Sarwari, Roya; Visser, Trudi P.; Hauer, Julia; Lagresle-Peyrou, Chantal; van der Velden, Guus; Malshetty, Vidyasagar; Cortes, Patricia; Jollet, Arnaud; Danos, Olivier; Cassani, Barbara; Zhang, Fang; Thrasher, Adrian J.; Fontana, Elena; Poliani, Pietro L.; Cavazzana, Marina; Verstegen, Monique M.A.; Villa, Anna; Wagemaker, Gerard
- 卷第133卷
- 期第4期
- 印刷ISSN0091-6749
- 文件大小2795.58KB
- 发表时间2014-04
- DOI10.1016/j.jaci.2013.10.009
- 页码1116-1123