Translational and Regulatory Challenges for Exon Skipping Therapies
Aartsma-Rus, Annemieke; Ferlini, Alessandra; Goemans, Nathalie; Pasmooij, Anna M.G.; Wells, Dominic J.; Bushby, Katerine; Vroom, Elizabeth; Balabanov, Pavel
- 期刊名称Human Gene Therapy
- 作者Aartsma-Rus, Annemieke; Ferlini, Alessandra; Goemans, Nathalie; Pasmooij, Anna M.G.; Wells, Dominic J.; Bushby, Katerine; Vroom, Elizabeth; Balabanov, Pavel
- 卷第25卷
- 期第10期
- 印刷ISSN1043-0342
- 电子ISSN1557-7422
- 文件大小238.42KB
- 发表时间2014-10
- DOI10.1089/hum.2014.086
- 页码885-892