Widespread correction of central nervous system disease after intracranial gene therapy in a feline model of Sandhoff disease
McCurdy, V J; Rockwell, H E; Arthur, J R; Bradbury, A M; Johnson, A K; Randle, A N; Brunson, B L; Hwang, M; Gray-Edwards, H L; Morrison, N E; Johnson, J A; Baker, H J; Cox, N R; Seyfried, T N; Sena-Esteves, M; Martin, D R
- 期刊名称Gene Therapy
- 作者McCurdy, V J; Rockwell, H E; Arthur, J R; Bradbury, A M; Johnson, A K; Randle, A N; Brunson, B L; Hwang, M; Gray-Edwards, H L; Morrison, N E; Johnson, J A; Baker, H J; Cox, N R; Seyfried, T N; Sena-Esteves, M; Martin, D R
- 卷第22卷
- 期第2期
- 印刷ISSN0969-7128
- 电子ISSN1476-5462
- 文件大小1494.10KB
- 发表时间2015-2
- DOI10.1038/gt.2014.108
- 页码181-189