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A comparison of AAV strategies distinguishes overlapping vectors for efficient systemic delivery of the 6.2 kb Dysferlin coding sequence

A comparison of AAV strategies distinguishes overlapping vectors for efficient systemic delivery of the 6.2 kb Dysferlin coding sequence

Pryadkina, Marina; Lostal, William; Bourg, Nathalie; Charton, Karine; Roudaut, Carinne; Hirsch, Matthew L; Richard, Isabelle
  • 期刊名称Molecular Therapy — Methods & Clinical Development
  • 作者Pryadkina, Marina; Lostal, William; Bourg, Nathalie; Charton, Karine; Roudaut, Carinne; Hirsch, Matthew L; Richard, Isabelle
  • 卷第2卷
  • DOI210.0000/www.nature.com/generic-499A1E0C0D9D
  • 电子ISSN2329-0501
  • 文件大小4595.42KB
  • 发表时间2015-3-25
  • DOI10.1038/mtm.2015.9
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