A comparison of AAV strategies distinguishes overlapping vectors for efficient systemic delivery of the 6.2 kb Dysferlin coding sequence
Pryadkina, Marina; Lostal, William; Bourg, Nathalie; Charton, Karine; Roudaut, Carinne; Hirsch, Matthew L; Richard, Isabelle
- 期刊名称Molecular Therapy — Methods & Clinical Development
- 作者Pryadkina, Marina; Lostal, William; Bourg, Nathalie; Charton, Karine; Roudaut, Carinne; Hirsch, Matthew L; Richard, Isabelle
- 卷第2卷
- DOI210.0000/www.nature.com/generic-499A1E0C0D9D
- 电子ISSN2329-0501
- 文件大小4595.42KB
- 发表时间2015-3-25
- DOI10.1038/mtm.2015.9