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Novel first-dose adverse drug reactions during a phase I trial of olipudase alfa (recombinant human acid sphingomyelinase) in adults with Niemann–Pick disease type B (acid sphingomyelinase deficiency)

Novel first-dose adverse drug reactions during a phase I trial of olipudase alfa (recombinant human acid sphingomyelinase) in adults with Niemann–Pick disease type B (acid sphingomyelinase deficiency)

McGovern, Margaret M.; Wasserstein, Melissa P.; Kirmse, Brian; Duvall, W. Lane; Schiano, Thomas; Thurberg, Beth L.; Richards, Susan; Cox, Gerald F.
  • 期刊名称Genetics in Medicine
  • 作者McGovern, Margaret M.; Wasserstein, Melissa P.; Kirmse, Brian; Duvall, W. Lane; Schiano, Thomas; Thurberg, Beth L.; Richards, Susan; Cox, Gerald F.
  • 印刷ISSN1098-3600
  • 电子ISSN1530-0366
  • 文件大小695.09KB
  • 发表时间2015-04-02
  • DOI10.1038/gim.2015.24
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