Delivery of an adeno-associated virus vector into CSF attenuates central nervous system disease in mucopolysaccharidosis type II mice
Hinderer, Christian; Katz, Nathan; Louboutin, Jean-Pierre; Bell, Peter; Yu, Hongwei; Nayal, Mohamad; Kozarsky, Karen F; O'Brien, W Timothy; Goode, Tamara; Wilson, James M.
- 期刊名称Human Gene Therapy
- 作者Hinderer, Christian; Katz, Nathan; Louboutin, Jean-Pierre; Bell, Peter; Yu, Hongwei; Nayal, Mohamad; Kozarsky, Karen F; O'Brien, W Timothy; Goode, Tamara; Wilson, James M.
- 印刷ISSN1043-0342
- 电子ISSN1557-7422
- 文件大小890.50KB
- 发表时间2016-08-10
- DOI10.1089/hum.2016.101