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Gene therapy using a miniCEP290 fragment delays photoreceptor degeneration in a mouse model of Leber congenital amaurosis (LCA)

Gene therapy using a miniCEP290 fragment delays photoreceptor degeneration in a mouse model of Leber congenital amaurosis (LCA)

Zhang, Wei; Li, Linjing; Su, Qin; Gao, Guangping; Khanna, Hemant
  • 期刊名称Human Gene Therapy
  • 作者Zhang, Wei; Li, Linjing; Su, Qin; Gao, Guangping; Khanna, Hemant
  • 印刷ISSN1043-0342
  • 电子ISSN1557-7422
  • 文件大小1897.47KB
  • 发表时间2017-07-05
  • DOI10.1089/hum.2017.049
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