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Efficient therapy for refractory Pompe disease by mannose 6-phosphate analogue grafting on acid α-glucosidase

Efficient therapy for refractory Pompe disease by mannose 6-phosphate analogue grafting on acid α-glucosidase

Basile, Ilaria; Da Silva, Afitz; El Cheikh, Khaled; Godefroy, Anastasia; Daurat, Morgane; Harmois, Alice; Perez, Marc; Caillaud, Catherine; Charbonné, Henry-Vincent; Pau, Bernard; Gary-Bobo, Magali; Morère, Alain; Garcia, Marcel; Maynadier, Marie
  • 期刊名称Journal of Controlled Release
  • 作者Basile, Ilaria; Da Silva, Afitz; El Cheikh, Khaled; Godefroy, Anastasia; Daurat, Morgane; Harmois, Alice; Perez, Marc; Caillaud, Catherine; Charbonné, Henry-Vincent; Pau, Bernard; Gary-Bobo, Magali; Morère, Alain; Garcia, Marcel; Maynadier, Marie
  • 印刷ISSN0168-3659
  • 文件大小1357.00KB
  • 发表时间2017-11
  • DOI10.1016/j.jconrel.2017.10.043
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