Ivacaftor treatment of cystic fibrosis in children aged 12 to <24 months and with a CFTR gating mutation (ARRIVAL): a phase 3 single-arm study
Rosenfeld, Margaret; Wainwright, Claire E; Higgins, Mark; Wang, Linda T; McKee, Charlotte; Campbell, Daniel; Tian, Simon; Schneider, Jennifer; Cunningham, Steve; Davies, Jane C; Rosenfeld, Margaret; Wainwright, Claire E.; Higgins, Mark; Wang, Linda T.; McKee, Charlotte; Campbell, Daniel; Tian, Simon; Schneider, Jennifer; Cunningham, Steve; Davies, Jane C.; Harris, William; Mogayzel, Peter; McCoy, Karen; Milla, Carlos; Rubenstein, Ronald; Walker, Seth; Black, Philip; Montgomery, Gregory; McColley, Susanna; Hiatt, Peter; Sawicki, Gregory; Rock, Michael; Aurora, Paul; Ratjen, Felix; Maitra, Anirban; Ives, Andrew; Gaillard, Erol; McNalley, Paul; Selvadurai, Hiranjan; Robinson, Philip
- 期刊名称The Lancet Respiratory Medicine
- 作者Rosenfeld, Margaret; Wainwright, Claire E; Higgins, Mark; Wang, Linda T; McKee, Charlotte; Campbell, Daniel; Tian, Simon; Schneider, Jennifer; Cunningham, Steve; Davies, Jane C; Rosenfeld, Margaret; Wainwright, Claire E.; Higgins, Mark; Wang, Linda T.; McKee, Charlotte; Campbell, Daniel; Tian, Simon; Schneider, Jennifer; Cunningham, Steve; Davies, Jane C.; Harris, William; Mogayzel, Peter; McCoy, Karen; Milla, Carlos; Rubenstein, Ronald; Walker, Seth; Black, Philip; Montgomery, Gregory; McColley, Susanna; Hiatt, Peter; Sawicki, Gregory; Rock, Michael; Aurora, Paul; Ratjen, Felix; Maitra, Anirban; Ives, Andrew; Gaillard, Erol; McNalley, Paul; Selvadurai, Hiranjan; Robinson, Philip
- 印刷ISSN2213-2600
- 文件大小1348.00KB
- 发表时间2018-6
- DOI10.1016/S2213-2600(18)30202-9