Efficacy of Multi-exon Skipping Treatment in Duchenne Muscular Dystrophy Dog Model Neonates
Lim, Kenji Rowel Q.; Echigoya, Yusuke; Nagata, Tetsuya; Kuraoka, Mutsuki; Kobayashi, Masanori; Aoki, Yoshitsugu; Partridge, Terence; Maruyama, Rika; Takeda, Shin’ichi; Yokota, Toshifumi
- 期刊名称Molecular Therapy
- 作者Lim, Kenji Rowel Q.; Echigoya, Yusuke; Nagata, Tetsuya; Kuraoka, Mutsuki; Kobayashi, Masanori; Aoki, Yoshitsugu; Partridge, Terence; Maruyama, Rika; Takeda, Shin’ichi; Yokota, Toshifumi
- 印刷ISSN1525-0016
- 文件大小2568.39KB
- 发表时间2018-10
- DOI10.1016/j.ymthe.2018.10.011