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Identification of Novel Antisense-Mediated Exon Skipping Targets in DYSF for Therapeutic Treatment of Dysferlinopathy

Identification of Novel Antisense-Mediated Exon Skipping Targets in DYSF for Therapeutic Treatment of Dysferlinopathy

Lee, Joshua J.A.; Maruyama, Rika; Duddy, William; Sakurai, Hidetoshi; Yokota, Toshifumi
  • 期刊名称Molecular Therapy - Nucleic Acids
  • 作者Lee, Joshua J.A.; Maruyama, Rika; Duddy, William; Sakurai, Hidetoshi; Yokota, Toshifumi
  • 卷第13卷
  • 印刷ISSN2162-2531
  • 文件大小1316.01KB
  • 发表时间2018-12
  • DOI10.1016/j.omtn.2018.10.004
  • 页码596-604
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