![Novel first-dose adverse drug reactions during a phase I trial of olipudase alfa (recombinant human acid sphingomyelinase) in adults with Niemann–Pick disease type B (acid sphingomyelinase deficiency)]()
Novel first-dose adverse drug reactions during a phase I trial of olipudase alfa (recombinant human acid sphingomyelinase) in adults with Niemann–Pick disease type B (acid sphingomyelinase deficiency)McGovern, Margaret M.; Wasserstein, Melissa P.; Kirmse, Brian; Duvall, W. Lane; Schiano, Thomas; Thurberg, Beth L.; Richards, Susan; Cox, Gerald F. · Genetics in Medicine · 2015