![Delivery of an adeno-associated virus vector into CSF attenuates central nervous system disease in mucopolysaccharidosis type II mice]()
Delivery of an adeno-associated virus vector into CSF attenuates central nervous system disease in mucopolysaccharidosis type II miceHinderer, Christian; Katz, Nathan; Louboutin, Jean-Pierre; Bell, Peter; Yu, Hongwei; Nayal, Mohamad; Kozarsky, Karen F; O'Brien, W Timothy; Goode, Tamara; Wilson, James M. · Human Gene Therapy · 2016